Cure SMA

Cure SMA has awarded a $140,000 research grant to Arthur Burghes, PhD, at The Ohio State University, for his project, "Defining the contribution of RNP assembly pathways to the SMA phenotype." Because of a genetic mutation in the SMN1 gene, individuals...

Cure SMA has awarded a $90,000 research grant to Antoine Cléry, PhD, at ETH Zurich for his project, "Novel approaches against spinal muscular atrophy by targeting splicing regulators." SMA is caused by a mutation in the SMN1 gene, which regulates the...

Cure SMA has awarded a $140,000 research grant to Christine Beattie, PhD, at the Ohio State University, for her project, "Identification of SMN:HuD bound RNAs critical for motor neuron development." Because of a genetic mutation in the SMN1 gene,...

Cure SMA has awarded a $140,000 research grant to Rashmi Kothary, MD, at the Ottawa Hospital Research Institute for his project, "Muscle satellite cell biology and muscle regeneration in Smn-depleted mice." Because of a genetic mutation, individuals with.

Cure SMA has awarded a $140,000 research grant to Megerditch Kiledjian, PhD, at Rutgers, The State University of New Jersey, for his project, "Novel Strategies to Increase SMN2 RNA.” Because of a genetic mutation in the SMN1 gene, individuals with SMA...

Cure SMA and Cytokinetics Inc. (Nasdaq: CYTK), a leading muscle biology company, today announced an expanded partnership to increase education, awareness and fundraising for spinal muscular atrophy (SMA).

Cure SMA has announced a new partnership with the District Policy Group, a boutique lobbying, public policy, and advocacy practice, to advocate for several key policy areas on behalf of the SMA community.

The SMA drug pipeline has grown dramatically in just over a decade. Of the 17 programs in the pipeline, seven of these are in clinical trials, and two of those are in Phase 3 clinical trials.

Cure SMA, the leading organization dedicated to the treatment and cure of spinal muscular atrophy (SMA), recently provided an additional $445,000 grant toward a gene therapy for SMA at Nationwide Children’s Hospital.

Cure SMA has awarded a $140,000 research grant to Chad Heatwole, MD, at the University of Rochester for his project, "Development of a Clinically Relevant Outcome Measure for SMA Therapeutic Trials." This grant is supported by funding from The Spinal...