Cure SMA

Cure SMA recently announced a new $315,000 drug discovery grant to the California Institute of Biomedical Research (CALIBR).

Cure SMA has awarded an $80,000 research grant to Linda Lowes, PT, PhD, at Nationwide Children’s Hospital for her project, “Development of An Innovative Outcome Measure to Define Disease Progression in SMA Type I for Use in the Home or Clinic.” As...

Spinal muscular atrophy (SMA) is the number one genetic cause of death for infants, and 1 in 50 people carry the genetic mutation that causes SMA. But even so, many people are not familiar with SMA. Thanks to the Cure SMA community, that is changing.

Cure SMA has awarded a $140,000 research grant to Mustafa Sahin, MD, PhD, at Boston Children’s Hospital for his project, “mTOR and Protein Synthesis in SMA.” Individuals with spinal muscular atrophy don’t produce survival motor neuron (SMN)...

Cure SMA has awarded a $140,000 research grant to Francesco Lotti, PhD, at Columbia University, for his project, "Role of Sumoylation in SMN Function and SMA Pathology." Survival motor neuron (SMN) protein is critical to the function of the nerves that...

Cure SMA, the leading organization in the US dedicated to the treatment and cure of spinal muscular atrophy (SMA), has issued a statement commending the US House of Representatives Energy and Commerce Committee for their release of the 21st Century Cures.

Cure SMA has announced a new $50,000 clinical care grant to Dr. Nilesh Mehta, for his project focusing on nutrition in spinal muscular atrophy (SMA).

Audrey Lewis founded Families of SMA, now Cure SMA, 30 years ago.